Victoria Gray was the first patient ever to be treated with the gene-editing tool CRISPR for sickle-cell disease.[1]
This marked the initial indication that a cure is attainable for individuals born with sickle-cell disease and another severe blood disorder, beta-thalassemia.[1]
- ^ a b Kaiser, Jocelyn (2020-12-11). "Tweaking genes with CRISPR or viruses fixes blood disorders". Science. 370 (6522): 1254–1255. Bibcode:2020Sci...370.1254K. doi:10.1126/science.370.6522.1254. ISSN 0036-8075. PMID 33303593. S2CID 228099693.